Gene-editing hope for muscular dystrophy
Scientists have for the first time used gene-editing to treat Duchenne muscular dystrophy in a large mammal, a significant step towards effective treatment for people with the disorder.The condition, which has no cure, leads to loss of muscle function and strength and ultimately an early death.But in a study on dogs, scientists were able to partially restore the key protein people with DMD cannot make.They hope in the future to test the technique in people. Green light for muscular dystrophy drug First gene-editing in human body attempt Duchenne muscular dystrophy (DMD) is the most common fatal genetic disease in children and almost entirely affects boys and young men - about 2,500 of them in the UK have the condition. Children born with the degenerative ...